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Clinical Trials
Leigh syndrome
A Phase 2B Randomized, Placebo-Controlled, Double-Blind Clinical Trial of EPI-743 in Children with Leigh Syndrome

Edison Pharmaceuticals is conducting a double-blind randomized placebo-controlled trial of EPI-743 for children with Leigh syndrome. The study is being conducted at four centers in the United States: Akron Children’s Hospital, Lucile Packard Children’s Hospital at Stanford, Seattle Children's Hospital, and Texas Children’s Hospital. For more information about trial enrollment please use the contact information below:

Study Sites

Akron Children’s Hospital
Akron, OH
Contact Hilary (Wolf) Tonni at htonni@chmca.org

Lucile Packard Children's Hospital, Stanford University Medical Center
Palo Alto, CA
Contact Katherine Connors at kconnors@stanford.edu

Seattle Children’s Hospital
Seattle, WA
Contact Laurie Guidry at laurie.guidry@seattlechildrens.org

Texas Children’s Hospital
Houston,TX
Contact Catherine Loffredo at catherine.loffredo@bcm.edu

Study Details

ClinicalTrials.gov

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Friedreich's ataxia
A Phase 2B Double-Blind, Placebo-Controlled, Clinical Trial of EPI-743 in Friedreich’s Ataxia

Edison Pharmaceuticals is conducting a phase 2B placebo-controlled trial of EPI-743 in patients with Friedreich’s ataxia. The study is planned to be conducted at three centers in the United States that include: Children’s Hospital of Philadelphia, University of California, Los Angeles, and University of South Florida. For more information about trial enrollment please see the contact information below:

Study Sites

Children's Hospital of Philadelphia
Philadelphia, PA
Contact Lauren Sayer at seyerl@email.chop.edu

University of California, Los Angeles
Los Angeles, CA
Contact Maria Casado at mcasado@mednet.ucla.edu

University of South Florida
Tampa, FL
Contact Kelly Sullivan at kbarber@health.usf.edu

Study Details

ClinicalTrials.gov

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